Regulators have opened a one-time gene therapy to some of the youngest patients with sickle cell disease. On July 1, 2026, ...

A new treatment for children aged 2 or older with sickle cell disease has been approved by the U.S. Food & Drug ...

The Food and Drug Administration recently approved gene therapy to treat sickle cell disease among children ages 2 and older, which a Nashville doctor described as a medical milestone.

Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.

By Yiqing Wang/WHRO State lawmakers have budgeted nearly $15 million over two years to help Virginia Medicaid cover gene ...

Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...

The U.S. Food and Drug Administration has issued a supplemental approval for Casgevy (exagamglogene autotemcel) for patients ...

Daniel Cressy, 23, says path leading to completion of curative gene therapy is his ‘greatest blessing’ ...

Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...

When Dr. Ambroise Wonkam walked into a panel on medical genetics out of curiosity, he had no idea it would shape the course of his career. Born in Cameroon, Wonkam has dedicated his career to studying ...

SAN DIEGO — A newly approved gene therapy product for sickle cell disease, lovotibeglogene autotemcel (lovo-cel, marketed as Lyfgenia), led to durable disease remissions for up to 5 years and almost ...

HBB-β S: An A greater than T point mutation results in the substitution of glutamate for valine in the sixth amino acid position (or seventh, if the… Development of SCD depends on whether the ...